Kevin Wake, 54, of Kansas City, has sickle cell disease. Every six weeks he receives blood transfusions that help alleviate…
Browsing: Gene
Scientists in Melbourne are making groundbreaking discoveries about the Hippo pathway at the molecular level, shedding light on how this…
Firefighters face more than just flames on the job. New research from the University of Arizona Mel and Enid Zuckerman…
Novartis Faces Challenges with Zolgensma Sales as Gene Therapy Market Struggles Business was thriving for Swiss pharmaceutical giant Novartis in…
Sarepta Therapeutics made a surprising announcement on Monday evening, revealing that it will be pausing all shipments of Elevidys, its…
The recent removal of Nicole Verdun, the FDA’s chief regulator of cell and gene therapies, stemmed from a disagreement with…
In our ongoing series on genetic medicine, we delve into the world of gene therapy and its current challenges. Recently,…
Advances in gene therapy are beginning to change the narrative for children with genetic diseases … More like Duchenne muscular…
The Trump administration’s impact on gene therapy has been a topic of interest for researchers, advocates, and industry executives. Recently,…
Until recently, even the most advanced gene therapies could only be given after a child was … More born—often racing…
