Sylvester Comprehensive Cancer Center, affiliated with the University of Miami Miller School of Medicine, has recently become a participant in…
Browsing: therapy
Novartis Faces Challenges with Zolgensma Sales as Gene Therapy Market Struggles Business was thriving for Swiss pharmaceutical giant Novartis in…
Sarepta Therapeutics made a surprising announcement on Monday evening, revealing that it will be pausing all shipments of Elevidys, its…
The recent removal of Nicole Verdun, the FDA’s chief regulator of cell and gene therapies, stemmed from a disagreement with…
The latest breakthrough in type 1 diabetes research has brought hope to twelve individuals who participated in an investigational off-the-shelf…
In our ongoing series on genetic medicine, we delve into the world of gene therapy and its current challenges. Recently,…
Advances in gene therapy are beginning to change the narrative for children with genetic diseases … More like Duchenne muscular…
The Trump administration’s impact on gene therapy has been a topic of interest for researchers, advocates, and industry executives. Recently,…
Until recently, even the most advanced gene therapies could only be given after a child was … More born—often racing…
As newborn screening and rapid DNA sequencing become routine, we are poised to catch and treat … More inherited diseases…
